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Considerations for evaluating the effectiveness and long-term outcome of enzyme replacement therapy in Pompe disease

Detalles Bibliográficos
Autor principal:	Cheon, Chong Kun
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Korean Pediatric Society 2019
Materias:	Editorial
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7027348/ https://www.ncbi.nlm.nih.gov/pubmed/31401827 http://dx.doi.org/10.3345/kjp.2018.07402

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