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Outcomes of Childhood Cholestasis in Alagille Syndrome: Results of a Multicenter Observational Study
Alagille syndrome (ALGS) is an autosomal dominant multisystem disorder with cholestasis as a defining clinical feature. We sought to characterize hepatic outcomes in a molecularly defined cohort of children with ALGS‐related cholestasis. Two hundred and ninety‐three participants with ALGS with nativ...
Autores principales: | Kamath, Binita M., Ye, Wen, Goodrich, Nathan P., Loomes, Kathleen M., Romero, Rene, Heubi, James E., Leung, Daniel H., Spinner, Nancy B., Piccoli, David A., Alonso, Estella M., Guthery, Stephen L., Karpen, Saul J., Mack, Cara L., Molleston, Jean P., Murray, Karen F., Rosenthal, Philip, Squires, James E., Teckman, Jeffrey, Wang, Kasper S., Thompson, Richard, Magee, John C., Sokol, Ronald J. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
John Wiley and Sons Inc.
2020
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7049675/ https://www.ncbi.nlm.nih.gov/pubmed/33313463 http://dx.doi.org/10.1002/hep4.1468 |
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