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The special considerations of gene therapy for mitochondrial diseases
The recent success of gene therapy across multiple clinical trials has inspired a great deal of hope regarding the treatment of previously intractable genetic diseases. This optimism has been extended to the prospect of gene therapy for mitochondrial disorders, which are not only particularly severe...
Autores principales: | Slone, Jesse, Huang, Taosheng |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Nature Publishing Group UK
2020
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7051955/ https://www.ncbi.nlm.nih.gov/pubmed/32140258 http://dx.doi.org/10.1038/s41525-020-0116-5 |
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