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New perspectives on the treatment of skeletal dysplasia
The last few decades have been marked by the identification of numerous genes implicated in genetic disorders, helping in the elucidation of the underlying pathophysiology of these conditions. This has allowed new therapeutic approaches to emerge such as cellular therapy, gene therapy, or pharmacolo...
Autores principales: | Marzin, Pauline, Cormier-Daire, Valérie |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
SAGE Publications
2020
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7054735/ https://www.ncbi.nlm.nih.gov/pubmed/32166011 http://dx.doi.org/10.1177/2042018820904016 |
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