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An Economic Evaluation of Voretigene Neparvovec for the Treatment of Biallelic RPE65-Mediated Inherited Retinal Dystrophies in the UK

INTRODUCTION: Voretigene neparvovec (VN) is a gene therapy and the first approved pharmacological treatment for biallelic RPE65-mediated inherited retinal dystrophies (IRD), a rare condition that starts in early life and causes vision to progressively deteriorate towards complete blindness. In a pha...

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Detalles Bibliográficos
Autores principales:	Viriato, Daniel, Bennett, Natalie, Sidhu, Raisa, Hancock, Elizabeth, Lomax, Hannah, Trueman, David, MacLaren, Robert E.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Springer Healthcare 2020
Materias:	Original Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7089725/ https://www.ncbi.nlm.nih.gov/pubmed/32034665 http://dx.doi.org/10.1007/s12325-020-01243-y

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