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Outcomes of hematopoietic stem cell transplantation for Hurler's syndrome in Europe: a risk factor analysis for graft failure
Hurler's syndrome (HS), the most severe form of mucopolysaccharidosis type-I, causes progressive deterioration of the central nervous system and death in childhood. Allogeneic stem cell transplantation (SCT) before the age of 2 years halts disease progression. Graft failure limits the success o...
Autores principales: | Boelens, J J, Wynn, R F, O'Meara, A, Veys, P, Bertrand, Y, Souillet, G, Wraith, J E, Fischer, A, Cavazzana-Calvo, M, Sykora, K W, Sedlacek, P, Rovelli, A, Uiterwaal, C S P M, Wulffraat, N |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Nature Publishing Group UK
2007
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7094454/ https://www.ncbi.nlm.nih.gov/pubmed/17529997 http://dx.doi.org/10.1038/sj.bmt.1705718 |
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