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Assessment of Activity of Daily Life in Mucopolysaccharidosis Type II Patients with Hematopoietic Stem Cell Transplantation

The effectiveness of hematopoietic stem cell transplantation (HSCT) for mucopolysaccharidosis type II (MPS II, Hunter disease) remains controversial although recent studies have shown HSCT provides more clinical impact. This study aims to evaluate the long-term effectiveness of HSCT using the activi...

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Detalles Bibliográficos
Autores principales:	Suzuki, Yasuyuki, Taylor, Madeleine, Orii, Kenji, Fukao, Toshiyuki, Orii, Tadao, Tomatsu, Shunji
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2020
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7168225/ https://www.ncbi.nlm.nih.gov/pubmed/31963134 http://dx.doi.org/10.3390/diagnostics10010046

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