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Gene Therapy for Cystic Fibrosis: Progress and Challenges of Genome Editing
Since the early days of its conceptualization and application, human gene transfer held the promise of a permanent solution to genetic diseases including cystic fibrosis (CF). This field went through alternated periods of enthusiasm and distrust. The development of refined technologies allowing site...
Autores principales: | Maule, Giulia, Arosio, Daniele, Cereseto, Anna |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2020
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7313467/ https://www.ncbi.nlm.nih.gov/pubmed/32486152 http://dx.doi.org/10.3390/ijms21113903 |
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