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Current and emerging treatment options for spinal muscular atrophy
Spinal muscular atrophy is one of the most common inherited neuromuscular conditions; our understanding of the genetic pathology and translational research coming from this insight has made significant progress over the past decade. This short review provides the background of the disease along with...
Autores principales: | Farooq, Faraz, MacKenzie, Alex E |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Dove
2015
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7337203/ https://www.ncbi.nlm.nih.gov/pubmed/32669914 http://dx.doi.org/10.2147/DNND.S48420 |
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