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Safety and Efficacy of the Sirolimus Gel for TSC Patients With Facial Skin Lesions in a Long-Term, Open-Label, Extension, Uncontrolled Clinical Trial

INTRODUCTION: Our previous clinical studies have demonstrated the short-term efficacy and safety of the sirolimus gel for patients with tuberous sclerosis complex (TSC). However, long-term clinical evidence is lacking. Our objective was to assess the safety and efficacy of long-term treatment with t...

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Detalles Bibliográficos
Autores principales: Wataya-Kaneda, Mari, Nagai, Hiroshi, Ohno, Yuuki, Yokozeki, Hiroo, Fujita, Yasuyuki, Niizeki, Hironori, Yoshida, Kazue, Ogai, Masaaki, Yoshida, Yuichi, Asahina, Akihiko, Fukai, Kazuyoshi, Tateishi, Chiharu, Hamada, Izumi, Takahata, Tatsuro, Shimizu, Kenji, Shimasaki, Shigeki, Murota, Hiroyuki
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer Healthcare 2020
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7367957/
https://www.ncbi.nlm.nih.gov/pubmed/32385845
http://dx.doi.org/10.1007/s13555-020-00387-7