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Are supplemental appraisal/reimbursement processes needed for rare disease treatments? An international comparison of country approaches
BACKGROUND: There is increasing recognition that conventional appraisal approaches may be unsuitable for assessing the value rare disease treatments (RDTs). This research examines what supplemental appraisal/reimbursement processes for RDTs are used internationally and how they can be characterised....
Autores principales: | Nicod, Elena, Whittal, Amanda, Drummond, Michael, Facey, Karen |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
BioMed Central
2020
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7370450/ https://www.ncbi.nlm.nih.gov/pubmed/32690107 http://dx.doi.org/10.1186/s13023-020-01462-0 |
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