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Cost Effectiveness of Voretigene Neparvovec for RPE65-Mediated Inherited Retinal Degeneration in Germany

PURPOSE: Voretigene Neparvovec-rzyl (VN) is the first available treatment for biallelic RPE65 mutation-associated inherited retinal degeneration, which is usually associated with infancy-onset severe visual impairment and complete blindness during the third life decade. We aim to estimate the cost e...

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Detalles Bibliográficos
Autores principales:	Uhrmann, Matthias Fritz, Lorenz, Birgit, Gissel, Christian
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	The Association for Research in Vision and Ophthalmology 2020
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7442871/ https://www.ncbi.nlm.nih.gov/pubmed/32879773 http://dx.doi.org/10.1167/tvst.9.9.17

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