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Quality of life data for individuals affected by spinal muscular atrophy: a baseline dataset from the Cure SMA Community Update Survey

BACKGROUND: Individuals and/or caregivers of individuals affected by spinal muscular atrophy (SMA) completed the 2019 Cure SMA Community Update Survey, online, assessing health-related quality of life (HRQoL), loss of work productivity, and fatigue using the Health Utilities Index Questionnaire (HUI...

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Detalles Bibliográficos
Autores principales:	Belter, Lisa, Cruz, Rosángel, Jarecki, Jill
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2020
Materias:	Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7447573/ https://www.ncbi.nlm.nih.gov/pubmed/32838797 http://dx.doi.org/10.1186/s13023-020-01498-2

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