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A Cross-Sectional Retrospective Study of Non-Splenectomized and Never-Treated Patients with Type 1 Gaucher Disease
Patients with type 1 Gaucher disease (GD1) present thrombocytopenia, anemia, organomegaly, and bone complications. Most experts consider that the less aggressive forms do not require specific treatment. However, little is known about the disease course of these forms. The objective of this cross-sec...
Autores principales: | Serratrice, Christine, Stirnemann, Jérôme, Berrahal, Amina, Belmatoug, Nadia, Camou, Fabrice, Caillaud, Catherine, Billette de Villemeur, Thierry, Dalbies, Florence, Cador, Bérengère, Froissart, Roseline, Masseau, Agathe, Brassier, Anaïs, Hivert, Bénédicte, Swiader, Laure, Bertchansky, Ivan, de Moreuil, Claire, Chabrol, Brigitte, Durieu, Isabelle, Leguy Seguin, Vanessa, Astudillo, Leonardo, Humbert, Sébastien, Pichard, Samia, Marcel, Catherine, Hau Rainsard, Isabelle, Bengherbia, Monia, Yousfi, Karima, Berger, Marc G. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2020
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7464688/ https://www.ncbi.nlm.nih.gov/pubmed/32708003 http://dx.doi.org/10.3390/jcm9082343 |
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