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Early clinical course after hematopoietic stem cell transplantation in children with juvenile metachromatic leukodystrophy
BACKGROUND: Long-term outcomes of hematopoietic stem cell transplantation (HSCT) in children with juvenile metachromatic leukodystrophy (MLD) have been investigated systematically, while short-term effects of HSCT on the course of the disease remain to be elucidated. RESULTS: In this study, the clin...
Autores principales: | Beschle, Judith, Döring, Michaela, Kehrer, Christiane, Raabe, Christa, Bayha, Ute, Strölin, Manuel, Böhringer, Judith, Bevot, Andrea, Kaiser, Nadja, Bender, Benjamin, Grimm, Alexander, Lang, Peter, Müller, Ingo, Krägeloh-Mann, Ingeborg, Groeschel, Samuel |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Springer Berlin Heidelberg
2020
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7483683/ https://www.ncbi.nlm.nih.gov/pubmed/32910272 http://dx.doi.org/10.1186/s40348-020-00103-7 |
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