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Development of a patient-reported outcome questionnaire for aplastic anemia and paroxysmal nocturnal hemoglobinuria (PRO-AA/PNH)

BACKGROUND: The introduction of new therapy modalities has significantly improved the outcome of aplastic anemia (AA) and paroxysmal nocturnal hemoglobinuria (PNH) patients. However, relatively little is known about the exact disease burden of AA/PNH since standardized assessments of symptoms includ...

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Detalles Bibliográficos
Autores principales:	Weisshaar, Kimmo, Ewald, Hannah, Halter, Jörg, Gerull, Sabine, Schönfeld, Sandra, Senft, Yuliya, Martinez, Maria, Leuppi-Taegtmeyer, Anne, Khanna, Nina, Maier, Birgit, Risitano, Antonio, Peffault de Latour, Regis, Tichelli, Andre, Passweg, Jakob, Drexler, Beatrice
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2020
Materias:	Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7495826/ https://www.ncbi.nlm.nih.gov/pubmed/32943103 http://dx.doi.org/10.1186/s13023-020-01532-3

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