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Gene Therapy for Neurodegenerative Diseases: Slowing Down the Ticking Clock
Gene therapy is an emerging and powerful therapeutic tool to deliver functional genetic material to cells in order to correct a defective gene. During the past decades, several studies have demonstrated the potential of AAV-based gene therapies for the treatment of neurodegenerative diseases. While...
Autores principales: | Martier, Raygene, Konstantinova, Pavlina |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Frontiers Media S.A.
2020
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7530328/ https://www.ncbi.nlm.nih.gov/pubmed/33071748 http://dx.doi.org/10.3389/fnins.2020.580179 |
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