Use of the patient-reported outcomes measurement information system (PROMIS®) to assess late-onset Pompe disease severity

BACKGROUND: Patient-Reported Outcomes provide an opportunity for patients to establish dialogue with pharmaceutical or biotechnology companies about their health conditions without interpretation by a clinician or anyone else. However, Patient-Reported Outcomes that can be widely applicable for use...

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Detalles Bibliográficos
Autores principales: Harfouche, Melodi, Kishnani, Priya S., Krusinska, Eva, Gault, Jamie, Sitaraman, Sheela, Sowinski, Amanda, Katz, Irina, Austin, Stephanie, Goldstein, Margi, Mulberg, Andrew E.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer International Publishing 2020
Materias:
Research
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7547055/
https://www.ncbi.nlm.nih.gov/pubmed/33034771
http://dx.doi.org/10.1186/s41687-020-00245-2

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