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Aspects of Gene Therapy Products Using Current Genome-Editing Technology in Japan

The development of genome-editing technology could lead to breakthrough gene therapy. Genome editing has made it possible to easily knock out or modify a target gene, while current gene therapy using a virus vector or plasmid hampering modification with respect to gene replacement therapies. Clinica...

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Detalles Bibliográficos
Autores principales:	Yamaguchi, Teruhide, Uchida, Eriko, Okada, Takashi, Ozawa, Keiya, Onodera, Masafumi, Kume, Akihiro, Shimada, Takashi, Takahashi, Satoru, Tani, Kenzaburo, Nasu, Yasutomo, Mashimo, Tomoji, Mizuguchi, Hiroyuki, Mitani, Kohnosuke, Maki, Kazushige
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Mary Ann Liebert, Inc., publishers 2020
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7585607/ https://www.ncbi.nlm.nih.gov/pubmed/32731837 http://dx.doi.org/10.1089/hum.2020.156

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