Inhibitor development in previously untreated patients with severe haemophilia: A comparison of included patients and outcomes between a clinical study and a registry‐based study

AIM: The aim of this study was to investigate whether a disease registry could serve as a suitable alternative to clinical studies to investigate safety of orphan drugs in children. METHODS: We used individual patient data from previously untreated patients (PUPs) with severe haemophilia A from the...

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Detalles Bibliográficos
Autores principales: Jonker, Carla J., Oude Rengerink, Katrien, Hoes, Arno W., Mol, Peter G. M., van den Berg, H. Marijke
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2020
Materias:
Original Articles
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7586966/
https://www.ncbi.nlm.nih.gov/pubmed/32627880
http://dx.doi.org/10.1111/hae.14100

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7586966/
https://www.ncbi.nlm.nih.gov/pubmed/32627880
http://dx.doi.org/10.1111/hae.14100

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