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Efficacy and safety of oral hydroxyurea in transfusion-dependent β-thalassaemia: a protocol for randomised double-blind controlled clinical trial

INTRODUCTION: Despite being one of the first diseases to be genetically characterised, β-thalassaemia remains a disorder without a cure in a majority of patients. Most patients with β-thalassaemia receive only supportive treatment and therefore have a poor quality of life and shorter life spans. Hyd...

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Detalles Bibliográficos
Autores principales:	Yasara, Nirmani, Wickramarathne, Nethmi, Mettananda, Chamila, Manamperi, Aresha, Premawardhena, Anuja, Mettananda, Sachith
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BMJ Publishing Group 2020
Materias:	Haematology (Incl Blood Transfusion)
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7592299/ https://www.ncbi.nlm.nih.gov/pubmed/33109679 http://dx.doi.org/10.1136/bmjopen-2020-041958

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