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Gene Editing for the Treatment of Primary Immunodeficiency Diseases

With conventional treatments for primary immunodeficiency diseases (PIDs), such as allogeneic stem cell transplantation or autologous gene therapy, still facing important challenges, the rapid development of genome editing technologies to more accurately correct the mutations underlying the onset of...

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Detalles Bibliográficos
Autores principales:	Rai, Rajeev, Thrasher, Adrian J., Cavazza, Alessia
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Mary Ann Liebert, Inc., publishers 2021
Materias:	Reviews
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7612852/ https://www.ncbi.nlm.nih.gov/pubmed/32935622 http://dx.doi.org/10.1089/hum.2020.185

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