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Turning genes into medicines—what have we learned from gene therapy drug development in the past decade?

Gene and cell therapy products approved over the past decade in Europe and North America have provided new therapeutic options for single gene disorders and for hematologic malignancies. Lessons learned, and limitations identified, are reviewed.

Detalles Bibliográficos
Autor principal:	High, Katherine A.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Nature Publishing Group UK 2020
Materias:	Comment
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7669843/ https://www.ncbi.nlm.nih.gov/pubmed/33199678 http://dx.doi.org/10.1038/s41467-020-19507-0

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