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New Therapeutics Options for Pediatric Neuromuscular Disorders
Neuromuscular disorders (NMDs) of Childhood onset are a genetically heterogeneous group of diseases affecting the anterior horn cell, the peripheral nerve, the neuromuscular junction, or the muscle. For many decades, treatment of NMDs has been exclusively symptomatic. But this has changed fundamenta...
Autores principales: | Flotats-Bastardas, Marina, Hahn, Andreas |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Frontiers Media S.A.
2020
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7719776/ https://www.ncbi.nlm.nih.gov/pubmed/33330280 http://dx.doi.org/10.3389/fped.2020.583877 |
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