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Current Genetic Survey and Potential Gene-Targeting Therapeutics for Neuromuscular Diseases

Neuromuscular diseases (NMDs) belong to a class of functional impairments that cause dysfunctions of the motor neuron-muscle functional axis components. Inherited monogenic neuromuscular disorders encompass both muscular dystrophies and motor neuron diseases. Understanding of their causative genetic...

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Detalles Bibliográficos
Autores principales:	Chiu, Wei, Hsun, Ya-Hsin, Chang, Kao-Jung, Yarmishyn, Aliaksandr A., Hsiao, Yu-Jer, Chien, Yueh, Chien, Chian-Shiu, Ma, Chun, Yang, Yi-Ping, Tsai, Ping-Hsing, Chiou, Shih-Hwa, Lin, Ting-Yi, Cheng, Hao-Min
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2020
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7767109/ https://www.ncbi.nlm.nih.gov/pubmed/33339321 http://dx.doi.org/10.3390/ijms21249589

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