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The development of the PlexiQoL: A patient‐reported outcome measure for adults with neurofibromatosis type 1‐associated plexiform neurofibromas

BACKGROUND: To develop and validate a patient‐reported outcome (PRO) measure of quality of life (QoL), specific to patients with Neurofibromatosis Type 1 (NF1)‐associated plexiform neurofibromas (pNFs), suitable for use in clinical efficacy trials. The study was conducted in parallel in the UK and U...

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Detalles Bibliográficos
Autores principales:	Heaney, Alice, Wilburn, Jeanette, Rouse, Matthew, Langmead, Shannon, Blakeley, Jaishri O., Huson, Susan, McKenna, Stephen P.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	John Wiley and Sons Inc. 2020
Materias:	Original Articles
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7767563/ https://www.ncbi.nlm.nih.gov/pubmed/33085177 http://dx.doi.org/10.1002/mgg3.1530

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