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Expanded circulating hematopoietic stem/ progenitor cells as novel cell source for the treatment of TCIRG1 osteopetrosis
Allogeneic hematopoietic stem cell transplantation is the treatment of choice for autosomal recessive osteopetrosis caused by defects in the TCIRG1 gene. Despite recent progress in conditioning, an important number of patients are not eligible for allogeneic stem cell transplantation because of the...
Autores principales: | Capo, Valentina, Penna, Sara, Merelli, Ivan, Barcella, Matteo, Scala, Serena, Basso-Ricci, Luca, Draghici, Elena, Palagano, Eleonora, Zonari, Erika, Desantis, Giacomo, Uva, Paolo, Cusano, Roberto, Sergi, Lucia Sergi, Crisafulli, Laura, Moshous, Despina, Stepensky, Polina, Drabko, Katarzyna, Kaya, Zühre, Unal, Ekrem, Gezdiric, Alper, Menna, Giuseppe, Serafini, Marta, Aiuti, Alessandro, Locatelli, Silvia Laura, Carlo-Stella, Carmelo, Schulz, Ansgar S., Ficara, Francesca, Sobacchi, Cristina, Gentner, Bernhard, Villa, Anna |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Fondazione Ferrata Storti
2020
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7776247/ https://www.ncbi.nlm.nih.gov/pubmed/31949009 http://dx.doi.org/10.3324/haematol.2019.238261 |
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