Assessment of rAAVrh.74.MHCK7.micro-dystrophin Gene Therapy Using Magnetic Resonance Imaging in Children With Duchenne Muscular Dystrophy

This case-control study uses magnetic resonance imaging and spectroscopy to evaluate the association between treatment with recombinant adeno-associated virus serotype rh74 (rAAVrh74) and muscle quality in children with Duchenne muscular dystrophy.

Detalles Bibliográficos
Autores principales: Willcocks, Rebecca J., Forbes, Sean C., Walter, Glenn A., Sweeney, Lee, Rodino-Klapac, Louise R., Mendell, Jerry R., Vandenborne, Krista
Formato: Online Artículo Texto
Lenguaje:English
Publicado: American Medical Association 2021
Materias:
Research Letter
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7783546/
https://www.ncbi.nlm.nih.gov/pubmed/33394000
http://dx.doi.org/10.1001/jamanetworkopen.2020.31851
Descripción
Sumario:This case-control study uses magnetic resonance imaging and spectroscopy to evaluate the association between treatment with recombinant adeno-associated virus serotype rh74 (rAAVrh74) and muscle quality in children with Duchenne muscular dystrophy.

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