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Motor unit changes in children with symptomatic spinal muscular atrophy treated with nusinersen

OBJECTIVES: To elucidate the motor unit response to intrathecal nusinersen in children with symptomatic spinal muscular atrophy (SMA) using a novel motor unit number estimation technique. METHODS: MScanFit MUNE studies were sequentially undertaken from the abductor pollicis brevis muscle after stimu...

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Detalles Bibliográficos
Autores principales:	Kariyawasam, Didu, D'Silva, Arlene, Howells, James, Herbert, Karen, Geelan-Small, Peter, Lin, Cindy Shin-Yi, Farrar, Michelle Anne
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BMJ Publishing Group 2021
Materias:	Neuromuscular
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7803907/ https://www.ncbi.nlm.nih.gov/pubmed/33106369 http://dx.doi.org/10.1136/jnnp-2020-324254

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