Ionizable lipid nanoparticles for in utero mRNA delivery

Clinical advances enable the prenatal diagnosis of genetic diseases that are candidates for gene and enzyme therapies such as messenger RNA (mRNA)–mediated protein replacement. Prenatal mRNA therapies can treat disease before the onset of irreversible pathology with high therapeutic efficacy and saf...

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Detalles Bibliográficos
Autores principales: Riley, Rachel S., Kashyap, Meghana V., Billingsley, Margaret M., White, Brandon, Alameh, Mohamad-Gabriel, Bose, Sourav K., Zoltick, Philip W., Li, Hiaying, Zhang, Rui, Cheng, Andrew Y., Weissman, Drew, Peranteau, William H., Mitchell, Michael J.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: American Association for the Advancement of Science 2021
Materias:
Research Articles
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7806221/
https://www.ncbi.nlm.nih.gov/pubmed/33523869
http://dx.doi.org/10.1126/sciadv.aba1028

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