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Cell Transplantation Combined with Recombinant Collagen Peptides for the Treatment of Fabry Disease

Fabry disease is caused by a decrease in or loss of the activity of alpha-galactosidase, which causes its substrates globotriaosylceramide (Gb3) and globotriaosylsphingosine (lyso-Gb3) to accumulate in cells throughout the body. This accumulation results in progressive kidney injury due to glomerulo...

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Detalles Bibliográficos
Autores principales:	Kami, Daisuke, Yamanami, Masashi, Tsukimura, Takahiro, Maeda, Hideki, Togawa, Tadayasu, Sakuraba, Hitoshi, Gojo, Satoshi
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	SAGE Publications 2020
Materias:	Original Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7873760/ https://www.ncbi.nlm.nih.gov/pubmed/33300391 http://dx.doi.org/10.1177/0963689720976362

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