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Evolving AAV-delivered therapeutics towards ultimate cures
Gene therapy has entered a new era after decades-long efforts, where the recombinant adeno-associated virus (AAV) has stood out as the most potent vector for in vivo gene transfer and demonstrated excellent efficacy and safety profiles in numerous preclinical and clinical studies. Since the first AA...
Autores principales: | He, Xiangjun, Urip, Brian Anugerah, Zhang, Zhenjie, Ngan, Chun Christopher, Feng, Bo |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Springer Berlin Heidelberg
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7885987/ https://www.ncbi.nlm.nih.gov/pubmed/33594520 http://dx.doi.org/10.1007/s00109-020-02034-2 |
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