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A primer to gene therapy: Progress, prospects, and problems
Genetic therapies based on gene addition have witnessed a variety of clinical successes and the first therapeutic products have been approved for clinical use. Moreover, innovative gene editing techniques are starting to offer new opportunities in which the mutations that underlie genetic diseases c...
Autores principales: | Zittersteijn, Hidde A., Gonçalves, Manuel A.F.V., Hoeben, Rob C. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
John Wiley & Sons, Inc.
2020
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7891367/ https://www.ncbi.nlm.nih.gov/pubmed/32510617 http://dx.doi.org/10.1002/jimd.12270 |
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