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Innovative Therapeutic Approaches for Duchenne Muscular Dystrophy
Duchenne muscular dystrophy (DMD) is the most common childhood muscular dystrophy affecting ~1:5000 live male births. Following the identification of pathogenic variations in the dystrophin gene in 1986, the underlining genotype/phenotype correlations emerged and the role of the dystrophin protein w...
Autores principales: | Fortunato, Fernanda, Rossi, Rachele, Falzarano, Maria Sofia, Ferlini, Alessandra |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7922390/ https://www.ncbi.nlm.nih.gov/pubmed/33671409 http://dx.doi.org/10.3390/jcm10040820 |
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