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Gene Therapies for Primary Immune Deficiencies

Gene therapy is an innovative treatment for Primary Immune Deficiencies (PIDs) that uses autologous hematopoietic stem cell transplantation to deliver stem cells with added or edited versions of the missing or malfunctioning gene that causes the PID. Initial studies of gene therapy for PIDs in the 1...

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Detalles Bibliográficos
Autores principales:	Kohn, Lisa A., Kohn, Donald B.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Frontiers Media S.A. 2021
Materias:	Immunology
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7946985/ https://www.ncbi.nlm.nih.gov/pubmed/33717203 http://dx.doi.org/10.3389/fimmu.2021.648951

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