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The Landscape of Non-Viral Gene Augmentation Strategies for Inherited Retinal Diseases
Inherited retinal diseases (IRDs) are a heterogeneous group of disorders causing progressive loss of vision, affecting approximately one in 1000 people worldwide. Gene augmentation therapy, which typically involves using adeno-associated viral vectors for delivery of healthy gene copies to affected...
Autores principales: | Toualbi, Lyes, Toms, Maria, Moosajee, Mariya |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7956638/ https://www.ncbi.nlm.nih.gov/pubmed/33652562 http://dx.doi.org/10.3390/ijms22052318 |
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