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Genome-Editing Strategies for Treating Human Retinal Degenerations
Inherited retinal degenerations (IRDs) are a leading cause of blindness. Although gene-supplementation therapies have been developed, they are only available for a small proportion of recessive IRD mutations. In contrast, genome editing using clustered-regularly interspaced short palindromic repeats...
Autores principales: | Quinn, Joel, Musa, Ayesha, Kantor, Ariel, McClements, Michelle E., Cehajic-Kapetanovic, Jasmina, MacLaren, Robert E., Xue, Kanmin |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Mary Ann Liebert, Inc., publishers
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7987357/ https://www.ncbi.nlm.nih.gov/pubmed/32993386 http://dx.doi.org/10.1089/hum.2020.231 |
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