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Systematic Review of N-of-1 Studies in Rare Genetic Neurodevelopmental Disorders: The Power of 1
OBJECTIVE: To improve the use of N-of-1 studies in rare genetic neurodevelopmental disorders, we systematically reviewed the literature and formulated recommendations for future studies. METHODS: The systematic review protocol was registered in the PROSPERO International Prospective Register of Syst...
Autores principales: | Müller, Annelieke R., Brands, Marion M.M.G., van de Ven, Peter M., Roes, Kit C.B., Cornel, Martina C., van Karnebeek, Clara D.M., Wijburg, Frits A., Daams, Joost G., Boot, Erik, van Eeghen, Agnies M. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Lippincott Williams & Wilkins
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8032375/ https://www.ncbi.nlm.nih.gov/pubmed/33504638 http://dx.doi.org/10.1212/WNL.0000000000011597 |
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