Cargando…
Therapeutic gene editing strategies using CRISPR-Cas9 for the β-hemoglobinopathies
With advancements in gene editing technologies, our ability to make precise and efficient modifications to the genome is increasing at a remarkable rate, paving the way for scientists and clinicians to uniquely treat a multitude of previously irremediable diseases. CRISPR-Cas9, short for clustered r...
Autores principales: | Papizan, James B., Porter, Shaina N., Sharma, Akshay, Pruett-Miller, Shondra M. |
---|---|
Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Editorial Department of Journal of Biomedical Research
2021
|
Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8038529/ https://www.ncbi.nlm.nih.gov/pubmed/33349624 http://dx.doi.org/10.7555/JBR.34.20200096 |
Ejemplares similares
-
A Survey of Validation Strategies for CRISPR-Cas9 Editing
por: Sentmanat, Monica F., et al.
Publicado: (2018) -
β-Hemoglobinopathies: The Test Bench for Genome Editing-Based Therapeutic Strategies
por: Barbarani, Gloria, et al.
Publicado: (2020) -
Positional cloning of quantitative trait nucleotides for blood pressure and cardiac QT-interval by targeted CRISPR/Cas9 editing of a novel long non-coding RNA
por: Cheng, Xi, et al.
Publicado: (2017) -
Precision Editing as a Therapeutic Approach for β-Hemoglobinopathies
por: Paschoudi, Kiriaki, et al.
Publicado: (2023) -
CRIS.py: A Versatile and High-throughput Analysis Program for CRISPR-based Genome Editing
por: Connelly, Jon P., et al.
Publicado: (2019)