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Muscle-Specific Promoters for Gene Therapy
Many genetic diseases that are responsible for muscular disorders have been described to date. Gene replacement therapy is a state-of-the-art strategy used to treat such diseases. In this approach, the functional copy of a gene is delivered to the affected tissues using viral vectors. There is an ur...
Autores principales: | Skopenkova, V. V., Egorova, T. V., Bardina, M. V. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
A.I. Gordeyev
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8084301/ https://www.ncbi.nlm.nih.gov/pubmed/33959386 http://dx.doi.org/10.32607/actanaturae.11063 |
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