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On the Corner of Models and Cure: Gene Editing in Cystic Fibrosis
Cystic fibrosis (CF) is a severe genetic disease for which curative treatment is still lacking. Next generation biotechnologies and more efficient cell-based and in vivo disease models are accelerating the development of novel therapies for CF. Gene editing tools, like CRISPR-based systems, can be u...
Autores principales: | Ensinck, Marjolein, Mottais, Angélique, Detry, Claire, Leal, Teresinha, Carlon, Marianne S. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Frontiers Media S.A.
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8111007/ https://www.ncbi.nlm.nih.gov/pubmed/33986686 http://dx.doi.org/10.3389/fphar.2021.662110 |
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