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A Discrete Choice Experiment to Derive Health Utilities for Aromatic L-Amino Acid Decarboxylase (AADC) Deficiency

PURPOSE: Deriving health utilities for rare medical conditions such as aromatic L-amino acid decarboxylase (AADC) deficiency poses challenges. The rarity of AADC deficiency and the fact that this genetic condition often presents in very young children means that robust utility values cannot be deriv...

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Detalles Bibliográficos
Autores principales:	Smith, Adam B, Hanbury, Andria, Whitty, Jennifer A, Buesch, Katharina
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Dove 2021
Materias:	Original Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8127000/ https://www.ncbi.nlm.nih.gov/pubmed/34012310 http://dx.doi.org/10.2147/PROM.S294628

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