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First open-label, single-arm, prospective study of real-world use of FIX replacement therapy in a predominantly pediatric hemophilia B population in China

BACKGROUND: Nonacog alfa (recombinant factor IX [FIX]) is approved in China for the control and prevention of bleeding events in patients with hemophilia B. This was the first study to assess prophylaxis and on-demand therapy with recombinant FIX replacement in a real-world setting in China. This st...

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Detalles Bibliográficos
Autores principales:	Yang, Renchi, Wu, Runhui, Sun, Jing, Sun, Feifei, Rupon, Jeremy, Huard, Francois, Korth-Bradley, Joan M., Xu, Lihong, Luo, Binyu, Liu, Yingxue Cathy, Rendo, Pablo
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Lippincott Williams & Wilkins 2021
Materias:	4800
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8154445/ https://www.ncbi.nlm.nih.gov/pubmed/34032739 http://dx.doi.org/10.1097/MD.0000000000026077

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