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Development of a New Quality of Life Measure for Duchenne Muscular Dystrophy Using Mixed Methods: The DMD-QoL

OBJECTIVE: Based on concerns about existing patient-reported outcome measures (PROMs) for assessing quality of life (QoL) in Duchenne muscular dystrophy (DMD), we describe the mixed methods development of a new QoL PROM for use in boys and men with DMD: the DMD-QoL. METHODS: The DMD-QoL was develope...

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Detalles Bibliográficos
Autores principales:	Powell, Philip A., Carlton, Jill, Rowen, Donna, Chandler, Fleur, Guglieri, Michela, Brazier, John E.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Lippincott Williams & Wilkins 2021
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8166440/ https://www.ncbi.nlm.nih.gov/pubmed/33785551 http://dx.doi.org/10.1212/WNL.0000000000011896

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