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Stepwise shortening of agalsidase beta infusion duration in Fabry disease: Clinical experience with infusion rate escalation protocol

BACKGROUND: Although enzyme replacement therapy with agalsidase beta resulted in a variety of clinical benefits, life‐long biweekly intravenous infusion may impact on patients’ quality of life. Moreover, regular infusions are time‐consuming: although a stepwise shortening of infusion duration is all...

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Detalles Bibliográficos
Autores principales:	Riccio, Eleonora, Zanfardino, Mario, Franzese, Monica, Capuano, Ivana, Buonanno, Pasquale, Ferreri, Lucia, Amicone, Maria, Pisani, Antonio
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	John Wiley and Sons Inc. 2021
Materias:	Original Articles
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8172210/ https://www.ncbi.nlm.nih.gov/pubmed/33755336 http://dx.doi.org/10.1002/mgg3.1659

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