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Emerging Therapies for Charcot-Marie-Tooth Inherited Neuropathies

Inherited neuropathies known as Charcot-Marie-Tooth (CMT) disease are genetically heterogeneous disorders affecting the peripheral nerves, causing significant and slowly progressive disability over the lifespan. The discovery of their diverse molecular genetic mechanisms over the past three decades...

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Detalles Bibliográficos
Autores principales:	Stavrou, Marina, Sargiannidou, Irene, Georgiou, Elena, Kagiava, Alexia, Kleopa, Kleopas A.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2021
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8199910/ https://www.ncbi.nlm.nih.gov/pubmed/34205075 http://dx.doi.org/10.3390/ijms22116048

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