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PROTECT VIII kids extension study: Long‐term safety and efficacy of BAY 94‐9027 (damoctocog alfa pegol) in children with severe haemophilia A

INTRODUCTION: BAY 94‐9027 (damoctocog alfa pegol; an extended half‐life PEGylated recombinant factor VIII [FVIII]) demonstrated efficacy and safety in previously treated paediatric patients (PTPs) aged <12 years with severe haemophilia A in the PROTECT VIII Kids study (NCT01775618). AIM: To evalu...

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Detalles Bibliográficos
Autores principales:	Mancuso, Maria Elisa, Biss, Tina, Fischer, Kathelijn, Maas Enriquez, Monika, Steele, MacGregor, Wang, Maria, Tseneklidou‐Stoeter, Despina, Ahuja, Sanjay, Kenet, Gili
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	John Wiley and Sons Inc. 2021
Materias:	Original Articles
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8251516/ https://www.ncbi.nlm.nih.gov/pubmed/33724632 http://dx.doi.org/10.1111/hae.14294

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