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Emerging Concepts in Vector Development for Glial Gene Therapy: Implications for Leukodystrophies
Central Nervous System (CNS) homeostasis and function rely on intercellular synchronization of metabolic pathways. Developmental and neurochemical imbalances arising from mutations are frequently associated with devastating and often intractable neurological dysfunction. In the absence of pharmacolo...
Autores principales: | von Jonquieres, Georg, Rae, Caroline D., Housley, Gary D. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Frontiers Media S.A.
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8258421/ https://www.ncbi.nlm.nih.gov/pubmed/34239416 http://dx.doi.org/10.3389/fncel.2021.661857 |
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