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Eliciting Health State Utilities for Aromatic L-Amino Acid Decarboxylase (AADC) Deficiency: A Vignette Study in France

PURPOSE: Health-related quality of life (HRQoL) is difficult to measure in rare diseases, especially in paediatric populations, yet capturing HRQoL is critical to evaluating treatment, including the cost-effectiveness of treatments. Given the ultra-rare nature of AADC deficiency indirect elicitation...

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Detalles Bibliográficos
Autores principales:	Smith, Adam B, Hanbury, Andria, Beitia Ortiz de Zarate, Igor, Hammes, Florence, de Pouvourville, Gerard, Buesch, Katharina
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Dove 2021
Materias:	Original Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8285298/ https://www.ncbi.nlm.nih.gov/pubmed/34285619 http://dx.doi.org/10.2147/PROM.S306228

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