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A new era for people with cystic fibrosis

Cystic fibrosis is the most prevalent inherited disease caused by a defect in the cystic fibrosis transmembrane conductance regulator (CFTR) gene. The impaired electrolyte homeostasis caused by the mutated or absent protein leads to symptoms in multiple organ systems. However, the pulmonary manifest...

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Detalles Bibliográficos
Autores principales:	Bierlaagh, Marlou C., Muilwijk, Danya, Beekman, Jeffrey M., van der Ent, Cornelis K.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Springer Berlin Heidelberg 2021
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8346380/ https://www.ncbi.nlm.nih.gov/pubmed/34213646 http://dx.doi.org/10.1007/s00431-021-04168-y

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